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Research Information

Methods of Research

Gene Therapy & Gene Editing

There are many methods in which scientists are using to approach research when it comes to HD. You may have heard of some of these terms, but what exactly do they mean? Can it work? As always, we remain cautiously optimistic, but we never lose hope. 

Gene Therapy

This method focuses on using genetic material to prevent or treat a disease. ASGCT does a great job of explaining how it all works, so we recommend checking out their website and watching out the video below.

Gene Editing

You may have heard this term quite a bit, especially if you have heard of research using CRISPR.  Gene editing is a type of gene therapy, but the difference is that it works to directly edit pieces of DNA within the cell. ASGCT also goes into detail about what gene editing looks like, you can check that out below!